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Chimeric protein repair of laminin polymerization ameliorates muscular dystrophy phenotype

Mutations in laminin α2-subunit (Lmα2, encoded by LAMA2) are linked to approximately 30% of congenital muscular dystrophy cases. Mice with a homozygous mutation in Lama2 (dy2J mice) express a nonpolymerizing form of laminin-211 (Lm211) and are a model for ambulatory-type Lmα2-deficient muscular dyst...

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Dades bibliogràfiques
Publicat a:J Clin Invest
Autors principals: McKee, Karen K., Crosson, Stephanie C., Meinen, Sarina, Reinhard, Judith R., Rüegg, Markus A., Yurchenco, Peter D.
Format: Artigo
Idioma:Inglês
Publicat: American Society for Clinical Investigation 2017
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC5330723/
https://ncbi.nlm.nih.gov/pubmed/28218617
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1172/JCI90854
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