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Efficacy and safety of deflazacort vs prednisone and placebo for Duchenne muscular dystrophy

OBJECTIVE: To assess safety and efficacy of deflazacort (DFZ) and prednisone (PRED) vs placebo in Duchenne muscular dystrophy (DMD). METHODS: This phase III, double-blind, randomized, placebo-controlled, multicenter study evaluated muscle strength among 196 boys aged 5–15 years with DMD during a 52-...

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Dades bibliogràfiques
Publicat a:Neurology
Autors principals: Griggs, Robert C., Miller, J. Phillip, Greenberg, Cheryl R., Fehlings, Darcy L., Pestronk, Alan, Mendell, Jerry R., Moxley, Richard T., King, Wendy, Kissel, John T., Cwik, Valerie, Vanasse, Michel, Florence, Julaine M., Pandya, Shree, Dubow, Jordan S., Meyer, James M.
Format: Artigo
Idioma:Inglês
Publicat: Lippincott Williams & Wilkins 2016
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC5109941/
https://ncbi.nlm.nih.gov/pubmed/27566742
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1212/WNL.0000000000003217
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