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Efficacy and safety of deflazacort vs prednisone and placebo for Duchenne muscular dystrophy
OBJECTIVE: To assess safety and efficacy of deflazacort (DFZ) and prednisone (PRED) vs placebo in Duchenne muscular dystrophy (DMD). METHODS: This phase III, double-blind, randomized, placebo-controlled, multicenter study evaluated muscle strength among 196 boys aged 5–15 years with DMD during a 52-...
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| Publicado no: | Neurology |
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| Main Authors: | , , , , , , , , , , , , , , |
| Formato: | Artigo |
| Idioma: | Inglês |
| Publicado em: |
Lippincott Williams & Wilkins
2016
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| Assuntos: | |
| Acesso em linha: | https://ncbi.nlm.nih.gov/pmc/articles/PMC5109941/ https://ncbi.nlm.nih.gov/pubmed/27566742 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1212/WNL.0000000000003217 |
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