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Comparison of Serum Pharmacodynamic Biomarkers in Prednisone-Versus Deflazacort-Treated Duchenne Muscular Dystrophy Boys

Prednisone (Pred) and Deflazacort (Dfz) are commonly used glucocorticoids (GCs) for Duchenne muscular dystrophy (DMD) treatment and management. While GCs are known to delay the loss of ambulation and motor abilities, chronic use can result in onerous side effects, e.g., weight gain, growth stunting,...

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Detalhes bibliográficos
Publicado no:J Pers Med
Main Authors: Tawalbeh, Shefa, Samsel, Alison, Gordish-Dressman, Heather, Hathout, Yetrib, Dang, Utkarsh J.
Formato: Artigo
Idioma:Inglês
Publicado em: MDPI 2020
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7720112/
https://ncbi.nlm.nih.gov/pubmed/33053810
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3390/jpm10040164
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