Загрузка...

Enzyme replacement with PEGylated cystathionine β-synthase ameliorates homocystinuria in murine model

Homocystinuria, which typically results from cystathionine β-synthase (CBS) deficiency, is the most common defect of sulfur amino acid metabolism. CBS condenses homocysteine and serine to cystathionine that is then converted to cysteine. Individuals with homocystinuria have markedly elevated plasma...

Полное описание

Сохранить в:
Библиографические подробности
Опубликовано в: :J Clin Invest
Главные авторы: Bublil, Erez M., Majtan, Tomas, Park, Insun, Carrillo, Richard S., Hůlková, Helena, Krijt, Jakub, Kožich, Viktor, Kraus, Jan P.
Формат: Artigo
Язык:Inglês
Опубликовано: American Society for Clinical Investigation 2016
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC4887166/
https://ncbi.nlm.nih.gov/pubmed/27183385
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1172/JCI85396
Метки: Добавить метку
Нет меток, Требуется 1-ая метка записи!