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Manufacturing of recombinant adeno-associated viral vectors for clinical trials
The ability to elicit robust and long-term transgene expression in vivo together with minimal immunogenicity and little to no toxicity are only a few features that make recombinant adeno-associated virus (rAAV) vectors ideally suited for many gene therapy applications. Successful preclinical studies...
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| Publicat a: | Mol Ther Methods Clin Dev |
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| Autors principals: | , |
| Format: | Artigo |
| Idioma: | Inglês |
| Publicat: |
Nature Publishing Group
2016
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| Matèries: | |
| Accés en línia: | https://ncbi.nlm.nih.gov/pmc/articles/PMC4804725/ https://ncbi.nlm.nih.gov/pubmed/27014711 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mtm.2016.2 |
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