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Analysis of conditional heterozygous STXBP1 mutations in human neurons

Heterozygous mutations in the syntaxin-binding protein 1 (STXBP1) gene, which encodes Munc18-1, a core component of the presynaptic membrane-fusion machinery, cause infantile early epileptic encephalopathy (Ohtahara syndrome), but it is unclear how a partial loss of Munc18-1 produces this severe cli...

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Dades bibliogràfiques
Publicat a:J Clin Invest
Autors principals: Patzke, Christopher, Han, Yan, Covy, Jason, Yi, Fei, Maxeiner, Stephan, Wernig, Marius, Südhof, Thomas C.
Format: Artigo
Idioma:Inglês
Publicat: American Society for Clinical Investigation 2015
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4588304/
https://ncbi.nlm.nih.gov/pubmed/26280581
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1172/JCI78612
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