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Halting progressive neurodegeneration in advanced retinitis pigmentosa

Hereditary retinal degenerative diseases, such as retinitis pigmentosa (RP), are characterized by the progressive loss of rod photoreceptors followed by loss of cones. While retinal gene therapy clinical trials demonstrated temporary improvement in visual function, this approach has yet to achieve s...

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Dades bibliogràfiques
Publicat a:J Clin Invest
Autors principals: Koch, Susanne F., Tsai, Yi-Ting, Duong, Jimmy K., Wu, Wen-Hsuan, Hsu, Chun-Wei, Wu, Wei-Pu, Bonet-Ponce, Luis, Lin, Chyuan-Sheng, Tsang, Stephen H.
Format: Artigo
Idioma:Inglês
Publicat: American Society for Clinical Investigation 2015
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4588299/
https://ncbi.nlm.nih.gov/pubmed/26301813
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1172/JCI82462
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