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Genetic rescue models refute nonautonomous rod cell death in retinitis pigmentosa

Retinitis pigmentosa (RP) is an inherited neurodegenerative disease, in which the death of mutant rod photoreceptors leads secondarily to the non-cell autonomous death of cone photoreceptors. Gene therapy is a promising treatment strategy. Unfortunately, current methods of gene delivery treat only a...

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Publicado en:Proc Natl Acad Sci U S A
Autores principales: Koch, Susanne F., Duong, Jimmy K., Hsu, Chun-Wei, Tsai, Yi-Ting, Lin, Chyuan-Sheng, Wahl-Schott, Christian A., Tsang, Stephen H.
Formato: Artigo
Lenguaje:Inglês
Publicado: National Academy of Sciences 2017
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC5441755/
https://ncbi.nlm.nih.gov/pubmed/28468800
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1073/pnas.1615394114
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