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Spinal muscular atrophy patient-derived motor neurons exhibit hyperexcitability

Spinal muscular atrophy (SMA) presents severe muscle weakness with limited motor neuron (MN) loss at an early stage, suggesting potential functional alterations in MNs that contribute to SMA symptom presentation. Using SMA induced pluripotent stem cells (iPSCs), we found that SMA MNs displayed hyper...

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Dettagli Bibliografici
Pubblicato in:Sci Rep
Autori principali: Liu, Huisheng, Lu, Jianfeng, Chen, Hong, Du, Zhongwei, Li, Xue-Jun, Zhang, Su-Chun
Natura: Artigo
Lingua:Inglês
Pubblicazione: Nature Publishing Group 2015
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4507262/
https://ncbi.nlm.nih.gov/pubmed/26190808
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/srep12189
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