Caricamento...

Rescue of the Stargardt phenotype in Abca4 knockout mice through inhibition of vitamin A dimerization

Stargardt disease, an ATP-binding cassette, subfamily A, member 4 (ABCA4)-related retinopathy, is a genetic condition characterized by the accelerated accumulation of lipofuscin in the retinal pigment epithelium, degeneration of the neuroretina, and loss of vision. No approved treatment exists. Here...

Descrizione completa

Salvato in:
Dettagli Bibliografici
Pubblicato in:Proc Natl Acad Sci U S A
Autori principali: Charbel Issa, Peter, Barnard, Alun R., Herrmann, Philipp, Washington, Ilyas, MacLaren, Robert E.
Natura: Artigo
Lingua:Inglês
Pubblicazione: National Academy of Sciences 2015
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4500285/
https://ncbi.nlm.nih.gov/pubmed/26106163
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1073/pnas.1506960112
Tags: Aggiungi Tag
Nessun Tag, puoi essere il primo ad aggiungerne! !