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Dendrimer Conjugates for Light-activated Delivery of Antisense Oligonucleotides

Therapeutic oligonucleotides, such as splice switching ONs (SSOs), provide opportunities for treating serious, life-threatening diseases. However, the development of ONs as therapeutic agents has progressed slowly, because difficult cytosolic delivery of SSOs into the cytosol and nucleus remains a m...

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Dettagli Bibliografici
Pubblicato in:RSC Adv
Autori principali: Yuan, Ahu, Hu, Yiqiao, Ming, Xin
Natura: Artigo
Lingua:Inglês
Pubblicazione: 2015
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4486491/
https://ncbi.nlm.nih.gov/pubmed/26146545
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1039/C5RA04091D
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