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Enzyme Replacement for Craniofacial Skeletal Defects and Craniosynostosis in Murine Hypophosphatasia

Hypophosphatasia (HPP) is an inborn-error-of-metabolism disorder characterized by deficient bone and tooth mineralization due to loss-of function mutations in the gene (Alpl) encoding tissue-nonspecific alkaline phosphatase (TNAP). Alpl(−/−) mice exhibit many characteristics seen in infantile HPP in...

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Dades bibliogràfiques
Publicat a:Bone
Autors principals: Liu, Jin, Campbell, Cassie, Nam, Hwa Kyung, Caron, Alexandre, Yadav, Manisha C, Millán, José Luis, Hatch, Nan E.
Format: Artigo
Idioma:Inglês
Publicat: 2015
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4466206/
https://ncbi.nlm.nih.gov/pubmed/25959417
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.bone.2015.05.005
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