Caricamento...

The novel Cln1(R151X) mouse model of infantile neuronal ceroid lipofuscinosis (INCL) for testing nonsense suppression therapy

The neuronal ceroid lipofuscinoses (NCLs), also known as Batten disease, are a group of autosomal recessive neurodegenerative disorders in children characterized by the progressive onset of seizures, blindness, motor and cognitive decline and premature death. Patients with mutations in CLN1 primaril...

Descrizione completa

Salvato in:
Dettagli Bibliografici
Pubblicato in:Hum Mol Genet
Autori principali: Miller, Jake N., Kovács, Attila D., Pearce, David A.
Natura: Artigo
Lingua:Inglês
Pubblicazione: Oxford University Press 2015
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4326326/
https://ncbi.nlm.nih.gov/pubmed/25205113
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/hmg/ddu428
Tags: Aggiungi Tag
Nessun Tag, puoi essere il primo ad aggiungerne! !