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Improving clinical efficacy of adeno associated vectors by rational capsid bioengineering

Adeno associated vectors (AAV) have shown considerable promise to treat various genetic disorders in both preclinical and clinical settings mainly because of its safety profile. However, efficient use of AAV to deliver genes in immune-competent sites like muscles and liver requires very high doses w...

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Dades bibliogràfiques
Publicat a:J Biomed Sci
Autor principal: Sen, Dwaipayan
Format: Artigo
Idioma:Inglês
Publicat: BioMed Central 2014
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4251935/
https://ncbi.nlm.nih.gov/pubmed/25425174
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s12929-014-0103-1
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