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Improving clinical efficacy of adeno associated vectors by rational capsid bioengineering

Adeno associated vectors (AAV) have shown considerable promise to treat various genetic disorders in both preclinical and clinical settings mainly because of its safety profile. However, efficient use of AAV to deliver genes in immune-competent sites like muscles and liver requires very high doses w...

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Detalhes bibliográficos
Publicado no:J Biomed Sci
Autor principal: Sen, Dwaipayan
Formato: Artigo
Idioma:Inglês
Publicado em: BioMed Central 2014
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC4251935/
https://ncbi.nlm.nih.gov/pubmed/25425174
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1186/s12929-014-0103-1
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