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Improvement of Cardiomyopathy After High-Fat Diet in Two Siblings with Glycogen Storage Disease Type III

Glycogenosis type III (GSD III) is an autosomal recessive disorder due to amylo-1,6-glucosidase deficiency. This disease causes limit dextrin storage in affected tissues: liver, skeletal muscles, and heart in GSD IIIa and only liver in GSD IIIb. Cardiomyopathy is quite frequent in GSD IIIa with vari...

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Dettagli Bibliografici
Pubblicato in:JIMD Rep
Autori principali: Brambilla, Alessandra, Mannarino, Savina, Pretese, Roberta, Gasperini, Serena, Galimberti, Cinzia, Parini, Rossella
Natura: Artigo
Lingua:Inglês
Pubblicazione: Springer Berlin Heidelberg 2014
Soggetti:
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4241197/
https://ncbi.nlm.nih.gov/pubmed/25308556
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/8904_2014_343
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