ロード中...

Design and evaluation of locked nucleic acid-based splice-switching oligonucleotides in vitro

Antisense-mediated modulation of pre-mRNA splicing is an attractive therapeutic strategy for genetic diseases. Currently, there are few examples of modulation of pre-mRNA splicing using locked nucleic acid (LNA) antisense oligonucleotides, and, in particular, no systematic study has addressed the op...

詳細記述

保存先:
書誌詳細
主要な著者: Shimo, Takenori, Tachibana, Keisuke, Saito, Kiwamu, Yoshida, Tokuyuki, Tomita, Erisa, Waki, Reiko, Yamamoto, Tsuyoshi, Doi, Takefumi, Inoue, Takao, Kawakami, Junji, Obika, Satoshi
フォーマット: Artigo
言語:Inglês
出版事項: Oxford University Press 2014
主題:
オンライン・アクセス:https://ncbi.nlm.nih.gov/pmc/articles/PMC4081108/
https://ncbi.nlm.nih.gov/pubmed/24935206
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/nar/gku512
タグ: タグ追加
タグなし, このレコードへの初めてのタグを付けませんか!