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Template-directed synthesis of a small molecule-antisense conjugate targeting an mRNA structure

The targeting of structural features in mRNA with specificity remains a great chemical challenge. A hairpin structure near exon 10 in the pre-mRNA encoding the tau protein controls its splicing, and dementia-causing mutations that disrupt this structure increase exon 10 splicing. We previously repor...

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Autori principali: Liu, Yang, Rodriguez, Lilia, Wolfe, Michael S.
Natura: Artigo
Lingua:Inglês
Pubblicazione: 2014
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC4079005/
https://ncbi.nlm.nih.gov/pubmed/24691171
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.bioorg.2014.03.001
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