Targeted gene transfer into ependymal cells through intraventricular injection of AAV1 vector and long-term enzyme replacement via the CSF

Lignende værker

• Enzyme replacement in the CSF to treat metachromatic leukodystrophy in mouse model using single intracerebroventricular injection of self-complementary AAV1 vector
  af: Hironaka, Kohei, et al.
  Udgivet: (2015)
• Distinct transduction profiles in the CNS via three injection routes of AAV9 and the application to generation of a neurodegenerative mouse model
  af: Fathul Huda, et al.
  Udgivet: (2014-01-01)
• Distinct transduction profiles in the CNS via three injection routes of AAV9 and the application to generation of a neurodegenerative mouse model
  af: Huda, Fathul, et al.
  Udgivet: (2014)
• Treatment of hypophosphatasia by muscle-directed expression of bone-targeted alkaline phosphatase via self-complementary AAV8 vector
  af: Nakamura-Takahashi, Aki, et al.
  Udgivet: (2016)
• Tyrosine triple mutated AAV2-BDNF gene therapy in a rat model of transient IOP elevation
  af: Igarashi, Tsutomu, et al.
  Udgivet: (2016)