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Targeted gene transfer into ependymal cells through intraventricular injection of AAV1 vector and long-term enzyme replacement via the CSF

Enzyme replacement via the cerebrospinal fluid (CSF) has been shown to ameliorate neurological symptoms in model animals with neuropathic metabolic disorders. Gene therapy via the CSF offers a means to achieve a long-term sustainable supply of therapeutic proteins within the central nervous system (...

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Autors principals: Yamazaki, Yoshiyuki, Hirai, Yukihiko, Miyake, Koichi, Shimada, Takashi
Format: Artigo
Idioma:Inglês
Publicat: Nature Publishing Group 2014
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4076682/
https://ncbi.nlm.nih.gov/pubmed/24981028
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/srep05506
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