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Baseline characteristics and disease burden in patients in the International Paroxysmal Nocturnal Hemoglobinuria Registry

Paroxysmal nocturnal hemoglobinuria is a rare, acquired disease associated with hemolytic anemia, bone marrow failure, thrombosis, and, frequently, poor quality of life. The International PNH Registry is a worldwide, observational, non-interventional study collecting safety, effectiveness, and quali...

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Autors principals: Schrezenmeier, Hubert, Muus, Petra, Socié, Gérard, Szer, Jeffrey, Urbano-Ispizua, Alvaro, Maciejewski, Jaroslaw P., Brodsky, Robert A., Bessler, Monica, Kanakura, Yuzuru, Rosse, Wendell, Khursigara, Gus, Bedrosian, Camille, Hillmen, Peter
Format: Artigo
Idioma:Inglês
Publicat: Ferrata Storti Foundation 2014
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC4008114/
https://ncbi.nlm.nih.gov/pubmed/24488565
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.3324/haematol.2013.093161
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