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Baseline clinical characteristics and disease burden in patients with paroxysmal nocturnal hemoglobinuria (PNH): updated analysis from the International PNH Registry

The International Paroxysmal Nocturnal Hemoglobinuria (PNH) Registry (NCT01374360) was initiated to optimize patient management by collecting data regarding disease burden, progression, and clinical outcomes. Herein, we report updated baseline demographics, clinical characteristics, disease burden d...

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Detalhes bibliográficos
Publicado no:Ann Hematol
Main Authors: Schrezenmeier, Hubert, Röth, Alexander, Araten, David J., Kanakura, Yuzuru, Larratt, Loree, Shammo, Jamile M., Wilson, Amanda, Shayan, Gilda, Maciejewski, Jaroslaw P.
Formato: Artigo
Idioma:Inglês
Publicado em: Springer Berlin Heidelberg 2020
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Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC7316848/
https://ncbi.nlm.nih.gov/pubmed/32390114
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s00277-020-04052-z
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