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Progesterone Antagonist Therapy in a Pelizaeus-Merzbacher Mouse Model
Pelizaeus-Merzbacher disease (PMD) is a severe hypomyelinating disease, characterized by ataxia, intellectual disability, epilepsy, and premature death. In the majority of cases, PMD is caused by duplication of PLP1 that is expressed in myelinating oligodendrocytes. Despite detailed knowledge of PLP...
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| Asıl Yazarlar: | , , , , , , , , , , |
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| Materyal Türü: | Artigo |
| Dil: | Inglês |
| Baskı/Yayın Bilgisi: |
Elsevier
2014
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| Konular: | |
| Online Erişim: | https://ncbi.nlm.nih.gov/pmc/articles/PMC3980417/ https://ncbi.nlm.nih.gov/pubmed/24680886 https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.ajhg.2014.03.001 |
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