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Translating Sleeping Beauty transposition into cellular therapies: Victories and challenges

Recent results confirm that long-term expression of therapeutic transgenes can be achieved by using a transposon-based system in primary stem cells and in vivo. Transposable elements are natural DNA transfer vehicles that are capable of efficient genomic insertion. The latest generation, Sleeping Be...

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Detalhes bibliográficos
Main Authors: Izsvák, Zsuzsanna, Hackett, Perry B., Cooper, Laurence J.N., Ivics, Zoltán
Formato: Artigo
Idioma:Inglês
Publicado em: 2010
Assuntos:
Acesso em linha:https://ncbi.nlm.nih.gov/pmc/articles/PMC3971908/
https://ncbi.nlm.nih.gov/pubmed/20652893
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1002/bies.201000027
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