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Hematopoietic Stem Cell Mobilization for Gene Therapy: Superior Mobilization by the Combination of Granulocyte–Colony Stimulating Factor Plus Plerixafor in Patients with β-Thalassemia Major

Successful stem cell gene therapy requires high numbers of genetically engineered hematopoietic stem cells collected using optimal mobilization strategies. Here we focus on stem cell mobilization strategies for thalassemia and present the results of a plerixafor-based mobilization trial with emphasi...

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Bibliografski detalji
Glavni autori: Yannaki, Evangelia, Karponi, Garyfalia, Zervou, Fani, Constantinou, Varnavas, Bouinta, Asimina, Tachynopoulou, Varvara, Kotta, Konstantina, Jonlin, Erica, Papayannopoulou, Thalia, Anagnostopoulos, Achilles, Stamatoyannopoulos, George
Format: Artigo
Jezik:Inglês
Izdano: Mary Ann Liebert, Inc. 2013
Teme:
Online pristup:https://ncbi.nlm.nih.gov/pmc/articles/PMC3787462/
https://ncbi.nlm.nih.gov/pubmed/24001178
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2013.163
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