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Gene Therapy for Misfolding Protein Diseases of the Central Nervous System

Protein aggregation as a result of misfolding is a common theme underlying neurodegenerative diseases. Accordingly, most recent studies aim to prevent protein misfolding and/or aggregation as a strategy to treat these pathologies. For instance, state-of-the-art approaches, such as silencing protein...

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Autors principals: San Sebastian, Waldy, Samaranch, Lluis, Kells, Adrian P., Forsayeth, John, Bankiewicz, Krystof S.
Format: Artigo
Idioma:Inglês
Publicat: Springer US 2013
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC3701766/
https://ncbi.nlm.nih.gov/pubmed/23700209
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1007/s13311-013-0191-8
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