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Drug Discovery for Duchenne Muscular Dystrophy via Utrophin Promoter Activation Screening

BACKGROUND: Duchenne muscular dystrophy (DMD) is a devastating muscle wasting disease caused by mutations in dystrophin, a muscle cytoskeletal protein. Utrophin is a homologue of dystrophin that can functionally compensate for its absence when expressed at increased levels in the myofibre, as shown...

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Autors principals: Moorwood, Catherine, Lozynska, Olga, Suri, Neha, Napper, Andrew D., Diamond, Scott L., Khurana, Tejvir S.
Format: Artigo
Idioma:Inglês
Publicat: Public Library of Science 2011
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC3197614/
https://ncbi.nlm.nih.gov/pubmed/22028826
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1371/journal.pone.0026169
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