The potential of utrophin and dystrophin combination therapies for Duchenne muscular dystrophy

Duchenne muscular dystrophy (DMD) is a lethal neuromuscular disorder caused by loss of dystrophin. Several therapeutic modalities are currently in clinical trials but none will achieve maximum functional rescue and full disease correction. Therefore, we explored the potential of combining the benefi...

Full description

Saved in:
Bibliographic Details
Published in:Hum Mol Genet
Main Authors: Guiraud, Simon, Edwards, Benjamin, Babbs, Arran, Squire, Sarah E, Berg, Adam, Moir, Lee, Wood, Matthew J, Davies, Kay E
Format: Artigo
Language:Inglês
Published: Oxford University Press 2019
Subjects:
General Article
Online Access:https://ncbi.nlm.nih.gov/pmc/articles/PMC6586144/
https://ncbi.nlm.nih.gov/pubmed/30990876
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/hmg/ddz049
Tags: Add Tag
No Tags, Be the first to tag this record!

Similar Items