The potential of utrophin and dystrophin combination therapies for Duchenne muscular dystrophy

Duchenne muscular dystrophy (DMD) is a lethal neuromuscular disorder caused by loss of dystrophin. Several therapeutic modalities are currently in clinical trials but none will achieve maximum functional rescue and full disease correction. Therefore, we explored the potential of combining the benefi...

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Bibliografiske detaljer
Udgivet i:Hum Mol Genet
Main Authors: Guiraud, Simon, Edwards, Benjamin, Babbs, Arran, Squire, Sarah E, Berg, Adam, Moir, Lee, Wood, Matthew J, Davies, Kay E
Format: Artigo
Sprog:Inglês
Udgivet: Oxford University Press 2019
Fag:
General Article
Online adgang:https://ncbi.nlm.nih.gov/pmc/articles/PMC6586144/
https://ncbi.nlm.nih.gov/pubmed/30990876
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/hmg/ddz049
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