Загрузка...

Drug Discovery for Duchenne Muscular Dystrophy via Utrophin Promoter Activation Screening

BACKGROUND: Duchenne muscular dystrophy (DMD) is a devastating muscle wasting disease caused by mutations in dystrophin, a muscle cytoskeletal protein. Utrophin is a homologue of dystrophin that can functionally compensate for its absence when expressed at increased levels in the myofibre, as shown...

Полное описание

Сохранить в:
Библиографические подробности
Главные авторы: Moorwood, Catherine, Lozynska, Olga, Suri, Neha, Napper, Andrew D., Diamond, Scott L., Khurana, Tejvir S.
Формат: Artigo
Язык:Inglês
Опубликовано: Public Library of Science 2011
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC3197614/
https://ncbi.nlm.nih.gov/pubmed/22028826
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1371/journal.pone.0026169
Метки: Добавить метку
Нет меток, Требуется 1-ая метка записи!