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Rescue From Respiratory Dysfunction by Transduction of Full-length Dystrophin to Diaphragm via the Peritoneal Cavity in Utrophin/Dystrophin Double Knockout Mice

Duchenne muscular dystrophy (DMD) is an inherited severe muscle wasting disorder with, thus far, no effective therapy. DMD causes respiratory and cardiac failure as well as muscle wastage. Among the various symptoms, respiratory insufficiency is a major cause of death in DMD patients at about 20 yea...

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Detaylı Bibliyografya
Asıl Yazarlar: Ishizaki, Masatoshi, Maeda, Yasushi, Kawano, Ryoko, Suga, Tomohiro, Uchida, Yuji, Uchino, Katsuhisa, Yamashita, Satoshi, Kimura, En, Uchino, Makoto
Materyal Türü: Artigo
Dil:Inglês
Baskı/Yayın Bilgisi: Nature Publishing Group 2011
Konular:
Online Erişim:https://ncbi.nlm.nih.gov/pmc/articles/PMC3129567/
https://ncbi.nlm.nih.gov/pubmed/21467999
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1038/mt.2011.58
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