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Mutant CAG repeats of Huntingtin transcript fold into hairpins, form nuclear foci and are targets for RNA interference

The CAG repeat expansions that occur in translated regions of specific genes can cause human genetic disorders known as polyglutamine (poly-Q)-triggered diseases. Huntington’s disease and spinobulbar muscular atrophy (SBMA) are examples of these diseases in which underlying mutations are localized n...

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Dettagli Bibliografici
Autori principali: de Mezer, Mateusz, Wojciechowska, Marzena, Napierala, Marek, Sobczak, Krzysztof, Krzyzosiak, Wlodzimierz J.
Natura: Artigo
Lingua:Inglês
Pubblicazione: Oxford University Press 2011
Soggetti:
RNA
Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC3089464/
https://ncbi.nlm.nih.gov/pubmed/21247881
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1093/nar/gkq1323
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