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Oligonucleotide therapeutic approaches for Huntington disease

Huntington disease is an autosomal dominant neurodegenerative disorder caused by a toxic expansion in the CAG repeat region of the huntingtin gene. Oligonucleotide approaches based on RNAi and antisense oligonucleotides provide promising new therapeutic strategies for direct intervention through red...

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Autors principals: Sah, Dinah W.Y., Aronin, Neil
Format: Artigo
Idioma:Inglês
Publicat: American Society for Clinical Investigation 2011
Matèries:
Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC3026739/
https://ncbi.nlm.nih.gov/pubmed/21285523
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1172/JCI45130
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