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Imaging Tetrahymena ribozyme splicing activity in single live mammalian cells

Tetrahymena ribozymes hold promise for repairing genetic disorders but are largely limited by their modest splicing efficiency and low production of final therapeutic proteins. Ribozyme evolution in intact living mammalian cells would greatly facilitate the discovery of new ribozyme variants with hi...

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Autors principals: Hasegawa, Sumitaka, Jackson, W. Coyt, Tsien, Roger Y., Rao, Jianghong
Format: Artigo
Idioma:Inglês
Publicat: National Academy of Sciences 2003
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Accés en línia:https://ncbi.nlm.nih.gov/pmc/articles/PMC299846/
https://ncbi.nlm.nih.gov/pubmed/14645710
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1073/pnas.2036553100
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