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Advances in the understanding of dyskeratosis congenita

Dyskeratosis congenita (DC) is a rare inherited syndrome exhibiting marked clinical and genetic heterogeneity. It is characterised by mucocutaneous abnormalities, bone marrow failure and a predisposition to cancer. Bone marrow failure is the principal cause of premature mortality. Studies over the l...

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Detalles Bibliográficos
Autores principales: Walne, Amanda J., Dokal, Inderjeet
Formato: Artigo
Lenguaje:Inglês
Publicado: 2009
Materias:
Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC2882229/
https://ncbi.nlm.nih.gov/pubmed/19208095
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1111/j.1365-2141.2009.07598.x
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