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Systemic Trans-Splicing Adeno-Associated Viral Delivery Efficiently Transduces the Heart of Adult mdx Mouse, a Model for Duchenne Muscular Dystrophy

Trans-splicing adeno-associated viral (tsAAV) vectors hold great promise for delivering large therapeutic genes. One potential application is in the treatment of Duchenne muscular dystrophy (DMD). In this case, it is necessary to transduce whole body muscle. We demonstrated body-wide AAV-9 tsAAV tra...

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Autori principali: Ghosh, Arkasubhra, Yue, Yongping, Shin, Jin-Hong, Duan, Dongsheng
Natura: Artigo
Lingua:Inglês
Pubblicazione: Mary Ann Liebert, Inc. 2009
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC2829465/
https://ncbi.nlm.nih.gov/pubmed/19627234
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2009.058
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