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Transient Transfection Methods for Clinical Adeno-Associated Viral Vector Production

Recombinant adeno-associated virus (AAV)-based vectors expressing therapeutic gene products have shown great potential for human gene therapy. One major challenge for translation of promising research to clinical development is the manufacture of sufficient quantities of AAV vectors that meet string...

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Dettagli Bibliografici
Autore principale: Wright, J. Fraser
Natura: Artigo
Lingua:Inglês
Pubblicazione: Mary Ann Liebert, Inc. 2009
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC2829280/
https://ncbi.nlm.nih.gov/pubmed/19438300
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1089/hum.2009.064
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