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Progress toward therapy with antisense-mediated splicing modulation

Antisense oligonucleotides (AO) or antisense RNA can complementarily bind to a target site in pre-mRNA and regulate gene splicing, either to restore gene function by reprogramming gene splicing or to inhibit gene expression by disrupting splicing. These two applications represent novel therapeutic s...

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Detalles Bibliográficos
Autores principales: Du, Liutao, Gatti, Richard A.
Formato: Artigo
Lenguaje:Inglês
Publicado: 2009
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Acceso en línea:https://ncbi.nlm.nih.gov/pmc/articles/PMC2753608/
https://ncbi.nlm.nih.gov/pubmed/19330717
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