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All known patient mutations in the ASH-RhoGAP domains of OCRL affect targeting and APPL1 binding

Mutations in the inositol 5-phosphatase OCRL are responsible for Lowe syndrome, an X-linked disorder characterized by bilateral cataracts, mental retardation, neonatal hypotonia, and renal Fanconi syndrome, and for Dent disease, another X-linked condition characterized by kidney reabsorption defects...

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Dettagli Bibliografici
Autori principali: McCrea, Heather J., Paradise, Summer, Tomasini, Livia, Addis, Maria, Melis, Maria Antonietta, De Matteis, Maria Antonietta, De Camilli, Pietro
Natura: Artigo
Lingua:Inglês
Pubblicazione: 2008
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Accesso online:https://ncbi.nlm.nih.gov/pmc/articles/PMC2442618/
https://ncbi.nlm.nih.gov/pubmed/18307981
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1016/j.bbrc.2008.02.067
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