Загрузка...

Small-molecule therapeutics for the treatment of glycolipid lysosomal storage disorders.

Glycosphingolipid (GSL) lysosomal storage disorders are a small but challenging group of human diseases to treat. Although these disorders appear to be monogenic in origin, where the catalytic activity of enzymes in GSL catabolism is impaired, the clinical presentation and severity of disease are he...

Полное описание

Сохранить в:
Библиографические подробности
Главные авторы: Butters, Terry D, Mellor, Howard R, Narita, Keishi, Dwek, Raymond A, Platt, Frances M
Формат: Artigo
Язык:Inglês
Опубликовано: 2003
Предметы:
Online-ссылка:https://ncbi.nlm.nih.gov/pmc/articles/PMC1693180/
https://ncbi.nlm.nih.gov/pubmed/12803927
https://ncbi.nlm.nih.govhttp://dx.doi.org/10.1098/rstb.2003.1278
Метки: Добавить метку
Нет меток, Требуется 1-ая метка записи!