ロード中...
Investigation of New Morpholino Oligomers to Increase Survival Motor Neuron Protein Levels in Spinal Muscular Atrophy
Spinal muscular atrophy (SMA) is an autosomal-recessive childhood motor neuron disease and the main genetic cause of infant mortality. SMA is caused by deletions or mutations in the survival motor neuron 1 (SMN1) gene, which results in SMN protein deficiency. Only one approved drug has recently beco...
保存先:
| 主要な著者: | , , , , , , |
|---|---|
| フォーマット: | Artigo |
| 言語: | Inglês |
| 出版事項: |
MDPI AG
2018-01-01
|
| シリーズ: | International Journal of Molecular Sciences |
| 主題: | |
| オンライン･アクセス: | http://www.mdpi.com/1422-0067/19/1/167 |
| タグ: |
タグ追加
タグなし, このレコードへの初めてのタグを付けませんか!
|