Utilization of the AAVS1 Safe Harbor Locus for Hematopoietic Specific Transgene Expression and Gene Knockdown in Human ES Cells

by Tiyaboonchai, Amita, Mac, Helen, Shamsedeen, Razveen, Mills, Jason A., Kishore, Siddarth, French, Deborah L., Gadue, Paul
Published 2014

AAV-Mediated Gene Therapy for Choroideremia: Preclinical Studies in Personalized Models

by Vasireddy, Vidyullatha, Mills, Jason A., Gaddameedi, Rajashekhar, Basner-Tschakarjan, Etiena, Kohnke, Monika, Black, Aaron D., Alexandrov, Krill, Zhou, Shangzhen, Maguire, Albert M., Chung, Daniel C., Mac, Helen, Sullivan, Lisa, Gadue, Paul, Bennicelli, Jeannette L., French, Deborah L., Bennett, Jean
Published 2013

Correction: AAV-Mediated Gene Therapy for Choroideremia: Preclinical Studies in Personalized Models

by Vasireddy, Vidyullatha, Mills, Jason A., Gaddameedi, Rajashekhar, Basner-Tschakarjan, Etiena, Kohnke, Monika, Black, Aaron D., Alexandrov, Krill, Zhou, Shangzhen, Maguire, Albert M., Chung, Daniel C., Mac, Helen, Sullivan, Lisa, Gadue, Paul, Bennicelli, Jeannette L., French, Deborah L., Bennett, Jean
Published in PLoS One (2015)

Clonal genetic and hematopoietic heterogeneity among human-induced pluripotent stem cell lines

by Mills, Jason A., Wang, Kai, Paluru, Prasuna, Ying, Lei, Lu, Lin, Galvão, Aline M., Xu, Dongbin, Yao, Yu, Sullivan, Spencer K., Sullivan, Lisa M., Mac, Helen, Omari, Amel, Jean, Jyh-Chang, Shen, Steve, Gower, Adam, Spira, Avi, Mostoslavsky, Gustavo, Kotton, Darrell N., French, Deborah L., Weiss, Mitchell J., Gadue, Paul
Published 2013