Utilization of the AAVS1 Safe Harbor Locus for Hematopoietic Specific Transgene Expression and Gene Knockdown in Human ES Cells

Autor Tiyaboonchai, Amita, Mac, Helen, Shamsedeen, Razveen, Mills, Jason A., Kishore, Siddarth, French, Deborah L., Gadue, Paul
Vydáno 2014

AAV-Mediated Gene Therapy for Choroideremia: Preclinical Studies in Personalized Models

Autor Vasireddy, Vidyullatha, Mills, Jason A., Gaddameedi, Rajashekhar, Basner-Tschakarjan, Etiena, Kohnke, Monika, Black, Aaron D., Alexandrov, Krill, Zhou, Shangzhen, Maguire, Albert M., Chung, Daniel C., Mac, Helen, Sullivan, Lisa, Gadue, Paul, Bennicelli, Jeannette L., French, Deborah L., Bennett, Jean
Vydáno 2013

Correction: AAV-Mediated Gene Therapy for Choroideremia: Preclinical Studies in Personalized Models

Autor Vasireddy, Vidyullatha, Mills, Jason A., Gaddameedi, Rajashekhar, Basner-Tschakarjan, Etiena, Kohnke, Monika, Black, Aaron D., Alexandrov, Krill, Zhou, Shangzhen, Maguire, Albert M., Chung, Daniel C., Mac, Helen, Sullivan, Lisa, Gadue, Paul, Bennicelli, Jeannette L., French, Deborah L., Bennett, Jean
Vydáno v PLoS One (2015)

Clonal genetic and hematopoietic heterogeneity among human-induced pluripotent stem cell lines

Autor Mills, Jason A., Wang, Kai, Paluru, Prasuna, Ying, Lei, Lu, Lin, Galvão, Aline M., Xu, Dongbin, Yao, Yu, Sullivan, Spencer K., Sullivan, Lisa M., Mac, Helen, Omari, Amel, Jean, Jyh-Chang, Shen, Steve, Gower, Adam, Spira, Avi, Mostoslavsky, Gustavo, Kotton, Darrell N., French, Deborah L., Weiss, Mitchell J., Gadue, Paul
Vydáno 2013