Severe neuromuscular denervation of clinically relevant muscles in a mouse model of spinal muscular atrophy

Por Ling, Karen K. Y., Gibbs, Rebecca M., Feng, Zhihua, Ko, Chien-Ping
Publicado em 2012

Synaptic Defects in the Spinal and Neuromuscular Circuitry in a Mouse Model of Spinal Muscular Atrophy

Por Ling, Karen K. Y., Lin, Ming-Yi, Zingg, Brian, Feng, Zhihua, Ko, Chien-Ping
Publicado em 2010

TSUNAMI: an antisense method to phenocopy splicing-associated diseases in animals

Por Sahashi, Kentaro, Hua, Yimin, Ling, Karen K.Y., Hung, Gene, Rigo, Frank, Horev, Guy, Katsuno, Masahisa, Sobue, Gen, Ko, Chien-Ping, Bennett, C. Frank, Krainer, Adrian R.
Publicado em 2012

Pathological impact of SMN2 mis-splicing in adult SMA mice

Por Sahashi, Kentaro, Ling, Karen K Y, Hua, Yimin, Wilkinson, John Erby, Nomakuchi, Tomoki, Rigo, Frank, Hung, Gene, Xu, David, Jiang, Ya-Ping, Lin, Richard Z, Ko, Chien-Ping, Bennett, C Frank, Krainer, Adrian R
Publicado em 2013

Pharmacokinetics, pharmacodynamics, and efficacy of a small-molecule SMN2 splicing modifier in mouse models of spinal muscular atrophy

Por Zhao, Xin, Feng, Zhihua, Ling, Karen K. Y., Mollin, Anna, Sheedy, Josephine, Yeh, Shirley, Petruska, Janet, Narasimhan, Jana, Dakka, Amal, Welch, Ellen M., Karp, Gary, Chen, Karen S., Metzger, Friedrich, Ratni, Hasane, Lotti, Francesco, Tisdale, Sarah, Naryshkin, Nikolai A., Pellizzoni, Livio, Paushkin, Sergey, Ko, Chien-Ping, Weetall, Marla
Publicado no Hum Mol Genet (2016)