Cell and Gene Therapy for Genetic Diseases: Inherited Disorders Affecting the Lung and Those Mimicking Sudden Infant Death Syndrome

מאת Keeler, Allison M., Flotte, Terence R.
יצא לאור 2012

Recombinant Adeno-Associated Virus Gene Therapy in Light of Luxturna (and Zolgensma and Glybera): Where Are We, and How Did We Get Here?

מאת Keeler, Allison M., Flotte, Terence R.
הוצא לאור ב Annu Rev Virol (2019)

CAR T-Cell Therapy: Progress and Prospects

מאת Wilkins, Olivia, Keeler, Allison M., Flotte, Terence R.
הוצא לאור ב Hum Gene Ther Methods (2017)

CRISPR/Cas-Dependent and Nuclease-Free In Vivo Therapeutic Gene Editing

מאת Dasgupta, Ishani, Flotte, Terence R., Keeler, Allison M.
הוצא לאור ב Hum Gene Ther (2021)

AAV9 Gene Replacement Therapy for Respiratory Insufficiency in Very-long Chain Acyl-CoA Dehydrogenase Deficiency

מאת Zieger, Marina, Keeler, Allison M., Flotte, Terence R., ElMallah, Mai K.
הוצא לאור ב J Inherit Metab Dis (2019)

Two-Plasmid Packaging System for Recombinant Adeno-Associated Virus

מאת Tang, Qiushi, Keeler, Allison M., Zhang, Songbo, Su, Qin, Lyu, Zhuoyao, Cheng, Yangfan, Gao, Guangping, Flotte, Terence R.
הוצא לאור ב Biores Open Access (2020)

Intralingual and Intrapleural AAV Gene Therapy Prolongs Survival in a SOD1 ALS Mouse Model

מאת Keeler, Allison M., Zieger, Marina, Semple, Carson, Pucci, Logan, Veinbachs, Alessandra, Brown, Robert H., Mueller, Christian, ElMallah, Mai K.
הוצא לאור ב Mol Ther Methods Clin Dev (2019)

Systemic AAV9 gene transfer in adult GM1 gangliosidosis mice reduces lysosomal storage in CNS and extends lifespan

מאת Weismann, Cara M., Ferreira, Jennifer, Keeler, Allison M., Su, Qin, Qui, Linghua, Shaffer, Scott A., Xu, Zuoshang, Gao, Guangping, Sena-Esteves, Miguel
הוצא לאור ב Hum Mol Genet (2015)

Restrictive Lung Disease in the Cu/Zn Superoxide-Dismutase 1 G93A Amyotrophic Lateral Sclerosis Mouse Model

מאת Stoica, Lorelei, Keeler, Allison M., Xiong, Lang, Kalfopoulos, Michael, Desrochers, Kaitlyn, Brown, Robert H., Sena-Esteves, Miguel, Flotte, Terence R., ElMallah, Mai K.
הוצא לאור ב Am J Respir Cell Mol Biol (2017)

Long-term Correction of Very Long-chain Acyl-CoA Dehydrogenase Deficiency in Mice Using AAV9 Gene Therapy

מאת Keeler, Allison M, Conlon, Thomas, Walter, Glenn, Zeng, Huadong, Shaffer, Scott A, Dungtao, Fu, Erger, Kirsten, Cossette, Travis, Tang, Qiushi, Mueller, Christian, Flotte, Terence R
יצא לאור 2012

Airway smooth muscle dysfunction in Pompe (Gaa(−/−)) mice

מאת Keeler, Allison M., Liu, Donghai, Zieger, Marina, Xiong, Lang, Salemi, Jeffrey, Bellvé, Karl, Byrne, Barry J., Fuller, David D., ZhuGe, Ronghua, ElMallah, Mai K.
הוצא לאור ב Am J Physiol Lung Cell Mol Physiol (2017)

Systemic Delivery of AAVB1-GAA Clears Glycogen and Prolongs Survival in a Mouse Model of Pompe Disease

מאת Keeler, Allison M., Zieger, Marina, Todeasa, Sophia H., McCall, Angela L., Gifford, Jennifer C., Birsak, Samantha, Choudhury, Sourav R., Byrne, Barry J., Sena-Esteves, Miguel, ElMallah, Mai K.
הוצא לאור ב Hum Gene Ther (2019)

Bridging from Intramuscular to Limb Perfusion Delivery of rAAV: Optimization in a Non-human Primate Study

מאת Gruntman, Alisha M., Gernoux, Gwladys, Tang, Qiushi, Ye, Guo-Jie, Knop, Dave R., Wang, Gensheng, Benson, Janet, Coleman, Kristen E., Keeler, Allison M., Mueller, Christian, Chicoine, Louis G., Chulay, Jeffrey D., Flotte, Terence R.
הוצא לאור ב Mol Ther Methods Clin Dev (2019)

Pollen-derived RNAs Are Found in the Human Circulation

מאת Koupenova, Milka, Mick, Eric, Corkrey, Heather A., Singh, Anupama, Tanriverdi, Selim E., Vitseva, Olga, Levy, Daniel, Keeler, Allison M., Ezzaty Mirhashemi, Marzieh, ElMallah, Mai K., Gerstein, Mark, Rozowsky, Joel, Tanriverdi, Kahraman, Freedman, Jane E.
הוצא לאור ב iScience (2019)

Novel Combinatorial MicroRNA-Binding Sites in AAV Vectors Synergistically Diminish Antigen Presentation and Transgene Immunity for Efficient and Stable Transduction

מאת Muhuri, Manish, Zhan, Wei, Maeda, Yukiko, Li, Jia, Lotun, Anoushka, Chen, Jennifer, Sylvia, Katelyn, Dasgupta, Ishani, Arjomandnejad, Motahareh, Nixon, Thomas, Keeler, Allison M., Manokaran, Sangeetha, He, Ran, Su, Qin, Tai, Phillip W. L., Gao, Guangping
הוצא לאור ב Front Immunol (2021)

Widespread Central Nervous System Gene Transfer and Silencing After Systemic Delivery of Novel AAV-AS Vector

מאת Choudhury, Sourav R, Harris, Anne F, Cabral, Damien J, Keeler, Allison M, Sapp, Ellen, Ferreira, Jennifer S, Gray-Edwards, Heather L, Johnson, Jacob A, Johnson, Aime K, Su, Qin, Stoica, Lorelei, DiFiglia, Marian, Aronin, Neil, Martin, Douglas R, Gao, Guangping, Sena-Esteves, Miguel
הוצא לאור ב Mol Ther (2016)