Treatment of Diabetes Insipidus with Propylthiouracil: Report of a Case

Por Kaye, Edward
Publicado em 1951

CLINICAL RESEARCH FOR RARE DISEASE: OPPORTUNITIES, CHALLENGES, AND SOLUTIONS

Por Griggs, Robert C., Batshaw, Mark, Dunkle, Mary, Gopal-Srivastava, Rashmi, Kaye, Edward, Krischer, Jeffrey, Nguyen, Tan, Paulus, Kathleen, Merkel, Peter A.
Publicado em 2008

Angiocentric CD3(+) T-Cell Infiltrates in Human Immunodeficiency Virus Type 1-Associated Central Nervous System Disease in Children

Por Katsetos, Christos D., Fincke, John E., Legido, Agustin, Lischner, Harold W., de Chadarevian, Jean-Pierre, Kaye, Edward M., Platsoucas, Chris D., Oleszak, Emilia L.
Publicado em 1999

Safety and Pharmacokinetic Profiles of Phosphorodiamidate Morpholino Oligomers with Activity against Ebola Virus and Marburg Virus: Results of Two Single-Ascending-Dose Studies

Por Heald, Alison E., Iversen, Patrick L., Saoud, Jay B., Sazani, Peter, Charleston, Jay S., Axtelle, Tim, Wong, Michael, Smith, William B., Vutikullird, Apinya, Kaye, Edward
Publicado no Antimicrob Agents Chemother (2014)

Antisense Oligonucleotides Delivered to the Mouse CNS Ameliorate Symptoms of Severe Spinal Muscular Atrophy

Por Passini, Marco A., Bu, Jie, Richards, Amy M., Kinnecom, Cathrine, Sardi, S. Pablo, Stanek, Lisa M., Hua, Yimin, Rigo, Frank, Matson, John, Hung, Gene, Kaye, Edward M., Shihabuddin, Lamya S., Krainer, Adrian R., Bennett, C. Frank, Cheng, Seng H.
Publicado em 2011

Longitudinal effect of eteplirsen versus historical control on ambulation in Duchenne muscular dystrophy

Por Mendell, Jerry R., Goemans, Nathalie, Lowes, Linda P., Alfano, Lindsay N., Berry, Katherine, Shao, James, Kaye, Edward M., Mercuri, Eugenio, Hamid, Hoda Abdel, Byrne, Barry J., Connolly, Anne M., Dracker, Robert A., Matthew Frank, L., Heydemann, Peter T., O'Brien, Kevin C., Sparks, Susan E., Specht, Linda A., Rodino‐Klapac, Louise, Sahenk, Zarife, Al‐Zaidy, Samiah, Cripe, Linda H., Lewis, Sarah, M, Pane, E, Mazzone, S, Messina, GL, Vita, Bertini, D Amico A, Casimiro, Berardinelli A, Y, Torrente, F, Magri, GP, Comi, G, Baranello, T, Mongini, A, Pini, R, Battini, E, Pegoraro, C, Bruno, L, Politano, S, Previtali
Publicado no Ann Neurol (2016)

Baseline results of the NeuroNEXT spinal muscular atrophy infant biomarker study

Por Kolb, Stephen J., Coffey, Christopher S., Yankey, Jon W., Krosschell, Kristin, Arnold, W. David, Rutkove, Seward B., Swoboda, Kathryn J., Reyna, Sandra P., Sakonju, Ai, Darras, Basil T., Shell, Richard, Kuntz, Nancy, Castro, Diana, Iannaccone, Susan T., Parsons, Julie, Connolly, Anne M., Chiriboga, Claudia A., McDonald, Craig, Burnette, W. Bryan, Werner, Klaus, Thangarajh, Mathula, Shieh, Perry B., Finanger, Erika, Cudkowicz, Merit E., McGovern, Michelle M., McNeil, D. Elizabeth, Finkel, Richard, Kaye, Edward, Kingsley, Allison, Renusch, Samantha R., McGovern, Vicki L., Wang, Xueqian, Zaworski, Phillip G., Prior, Thomas W., Burghes, Arthur H.M., Bartlett, Amy, Kissel, John T.
Publicado no Ann Clin Transl Neurol (2016)

Natural History of Infantile-Onset Spinal Muscular Atrophy

Por Kolb, Stephen J., Coffey, Christopher S., Yankey, Jon W., Krosschell, Kristin, Arnold, W. David, Rutkove, Seward B., Swoboda, Kathryn J., Reyna, Sandra P., Sakonju, Ai, Darras, Basil T., Shell, Richard, Kuntz, Nancy, Castro, Diana, Parsons, Julie, Connolly, Anne M., Chiriboga, Claudia A., McDonald, Craig, Burnette, W. Bryan, Werner, Klaus, Thangarajh, Mathula, Shieh, Perry B., Finanger, Erika, Cudkowicz, Merit E., McGovern, Michelle M., McNeil, D. Elizabeth, Finkel, Richard, Iannaccone, Susan T., Kaye, Edward, Kingsley, Allison, Renusch, Samantha R., McGovern, Vicki L., Wang, Xueqian, Zaworski, Phillip G., Prior, Thomas W., Burghes, Arthur H.M., Bartlett, Amy, Kissel, John T.
Publicado no Ann Neurol (2017)