Asialoglycoprotein receptor 1 mediates productive uptake of N-acetylgalactosamine-conjugated and unconjugated phosphorothioate antisense oligonucleotides into liver hepatocytes

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Reduction in ocular complement factor B protein in mice and monkeys by systemic administration of factor B antisense oligonucleotide

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Cyhoeddwyd yn Mol Vis (2017)