Systemic RNAi Delivery to the Muscles of ROSA26 Mice Reduces lacZ Expression

Por Wei, Jessica, Chamberlain, Joel R.
Publicado em 2014

Progress toward Gene Therapy for Duchenne Muscular Dystrophy

Por Chamberlain, Joel R., Chamberlain, Jeffrey S.
Publicado no Mol Ther (2017)

Purification and characterization of the nuclear RNase P holoenzyme complex reveals extensive subunit overlap with RNase MRP

Por Chamberlain, Joel R., Lee, Yoon, Lane, William S., Engelke, David R.
Publicado em 1998

Molecular and cellular adaptations to chronic myotendinous strain injury in mdx mice expressing a truncated dystrophin

Por Banks, Glen B., Combs, Ariana C., Chamberlain, Joel R., Chamberlain, Jeffrey S.
Publicado em 2008

5′ Processing of tRNA Precursors Can Be Modulated by the Human La Antigen Phosphoprotein

Por Fan, Hao, Goodier, John L., Chamberlain, Joel R., Engelke, David R., Maraia, Richard J.
Publicado em 1998

Gene Targeting of Mutant COL1A2 Alleles in Mesenchymal Stem Cells From Individuals With Osteogenesis Imperfecta

Por Chamberlain, Joel R, Deyle, David R, Schwarze, Ulrike, Wang, Peirong, Hirata, Yi Li, Byers, Peter H, Russell, David W
Publicado em 2007

Therapeutic impact of systemic AAV-mediated RNA interference in a mouse model of myotonic dystrophy

Por Bisset, Darren R., Stepniak-Konieczna, Ewa A., Zavaljevski, Maja, Wei, Jessica, Carter, Gregory T., Weiss, Michael D., Chamberlain, Joel R.
Publicado no Hum Mol Genet (2015)

Adeno-associated viral vectors do not efficiently target muscle satellite cells

Por Arnett, Andrea LH, Konieczny, Patryk, Ramos, Julian N, Hall, John, Odom, Guy, Yablonka-Reuveni, Zipora, Chamberlain, Joel R, Chamberlain, Jeffrey S
Publicado no Mol Ther Methods Clin Dev (2014)

AAV6-mediated Systemic shRNA Delivery Reverses Disease in a Mouse Model of Facioscapulohumeral Muscular Dystrophy

Por Bortolanza, Sergia, Nonis, Alessandro, Sanvito, Francesca, Maciotta, Simona, Sitia, Giovanni, Wei, Jessica, Torrente, Yvan, Di Serio, Clelia, Chamberlain, Joel R, Gabellini, Davide
Publicado em 2011

Muscle-specific CRISPR/Cas9 dystrophin gene editing ameliorates pathophysiology in a mouse model for Duchenne muscular dystrophy

Por Bengtsson, Niclas E., Hall, John K., Odom, Guy L., Phelps, Michael P., Andrus, Colin R., Hawkins, R. David, Hauschka, Stephen D., Chamberlain, Joel R., Chamberlain, Jeffrey S.
Publicado no Nat Commun (2017)

Corrigendum: Muscle-specific CRISPR/Cas9 dystrophin gene editing ameliorates pathophysiology in a mouse model for Duchenne muscular dystrophy

Por Bengtsson, Niclas E., Hall, John K., Odom, Guy L., Phelps, Michael P., Andrus, Colin R., Hawkins, R. David, Hauschka, Stephen D., Chamberlain, Joel R., Chamberlain, Jeffrey S.
Publicado no Nat Commun (2017)

Animal Models of Muscular Dystrophy

Por Ng, Rainer, Banks, Glen B., Hall, John K., Muir, Lindsey A., Ramos, Julian N., Wicki, Jacqueline, Odom, Guy L., Konieczny, Patryk, Seto, Jane, Chamberlain, Joel R., Chamberlain, Jeffrey S.
Publicado no Prog Mol Biol Transl Sci (2012)