Lysosomal storage disease: gene therapy on both sides of the blood-brain barrier

Por Aronovich, Elena L., Hackett, Perry B.
Publicado no Mol Genet Metab (2014)

Rational Design for Enhanced Gene Therapy with DNA Transposons

Por Hackett, Perry B, Aronovich, Elena L
Publicado no Mol Ther (2014)

The Sleeping Beauty transposon system: a non-viral vector for gene therapy

Por Aronovich, Elena L., McIvor, R. Scott, Hackett, Perry B.
Publicado em 2011

Excision of Sleeping Beauty transposons: parameters and applications to gene therapy

Por Liu, Geyi, Aronovich, Elena L., Cui, Zongbin, Whitley, Chester B., Hackett, Perry B.
Publicado em 2004

Duration of Expression and Activity of Sleeping Beauty Transposase in mouse liver following hydrodynamic DNA delivery

Por Bell, Jason B, Aronovich, Elena L, Schreifels, Jeffrey M, Beadnell, Thomas C, Hackett, Perry B
Publicado em 2010

Quantitative Analysis of α-L-Iduronidase Expression in Immunocompetent Mice Treated with the Sleeping Beauty Transposon System

Por Aronovich, Elena L., Hall, Bryan C., Bell, Jason B., McIvor, R. Scott, Hackett, Perry B.
Publicado em 2013

NMR structural analysis of Sleeping Beauty transposase binding to DNA

Por E Carpentier, Claire, Schreifels, Jeffrey M, Aronovich, Elena L, Carlson, Daniel F, Hackett, Perry B, Nesmelova, Irina V
Publicado em 2014

Preferential delivery of the Sleeping Beauty transposon system to livers of mice by hydrodynamic injection

Por Bell, Jason B, Podetz-Pedersen, Kelly M, Aronovich, Elena L, Belur, Lalitha R, McIvor, R Scott, Hackett, Perry B
Publicado em 2007

Efficacy and Safety of Sleeping Beauty Transposon-Mediated Gene Transfer in Preclinical Animal Studies

Por Hackett, Perry B., Aronovich, Elena L., Hunter, David, Urness, Myra, Bell, Jason B., Kass, Steven J., Cooper, Laurence J.N., McIvor, R. Scott
Publicado em 2011

Prolonged expression of a lysosomal enzyme in mouse liver after Sleeping Beauty transposon-mediated gene delivery: implications for non-viral gene therapy of mucopolysaccharidoses

Por Aronovich, Elena L., Bell, Jason B., Belur, Lalitha R., Gunther, Roland, Koniar, Brenda, Erickson, David C. C., Schachern, Patricia A., Matise, Ilze, McIvor, R. Scott, Whitley, Chester B., Hackett, Perry B.
Publicado em 2007

Systemic Correction of Storage Disease in MPS I NOD/SCID Mice Using the Sleeping Beauty Transposon System

Por Aronovich, Elena L, Bell, Jason B, Khan, Shaukat A, Belur, Lalitha R, Gunther, Roland, Koniar, Brenda, Schachern, Patricia A, Parker, Josh B, Carlson, Cathy S, Whitley, Chester B, McIvor, R Scott, Gupta, Pankaj, Hackett, Perry B
Publicado em 2009