Gene Therapy with Hematopoietic Stem Cells: The Diseased Bone Marrow's Point of View

由 Cavazzana, Marina, Ribeil, Jean-Antoine, Lagresle-Peyrou, Chantal, André-Schmutz, Isabelle
發表在 Stem Cells Dev (2017)

Fetal consequences of maternal antiretroviral nucleoside reverse transcriptase inhibitor (NRTI) use in human and non-human primate pregnancy

由 Poirier, Miriam C., Gibbons, Alexander T., Rugeles, Maria T., Andre-Schmutz, Isabelle, Blanche, Stephane
發表在 Curr Opin Pediatr (2015)

Gene Therapy for X-Linked Severe Combined Immunodeficiency: Where Do We Stand?

由 Cavazzana, Marina, Six, Emmanuelle, Lagresle-Peyrou, Chantal, André-Schmutz, Isabelle, Hacein-Bey-Abina, Salima
發表在 Hum Gene Ther (2016)

A Nontoxic Transduction Enhancer Enables Highly Efficient Lentiviral Transduction of Primary Murine T Cells and Hematopoietic Stem Cells

由 Delville, Marianne, Soheili, Tayebeh, Bellier, Florence, Durand, Amandine, Denis, Adeline, Lagresle-Peyrou, Chantal, Cavazzana, Marina, Andre-Schmutz, Isabelle, Six, Emmanuelle
發表在 Mol Ther Methods Clin Dev (2018)

Hematopoietic Stem Cell Transplant for the Treatment of X-MAID

由 Henrickson, Sarah E., Andre-Schmutz, Isabelle, Lagresle-Peyrou, Chantal, Deardorff, Matthew A., Jyonouchi, Harumi, Neven, Benedicte, Bunin, Nancy, Heimall, Jennifer R.
發表在 Front Pediatr (2019)

CXCR4-Related Increase of Circulating Human Lymphoid Progenitors after Allogeneic Hematopoietic Stem Cell Transplantation

由 Glauzy, Salomé, André-Schmutz, Isabelle, Larghero, Jérôme, Ezine, Sophie, de Latour, Régis Peffault, Moins-Teisserenc, Hélène, Servais, Sophie, Robin, Marie, Socié, Gérard, Clave, Emmanuel, Toubert, Antoine
出版 2014

Comparing genotoxic signatures in cord blood cells from neonates exposed in utero to zidovudine or tenofovir

由 Vivanti, Alexandre, Soheili, Tayebeh S., Cuccuini, Wendy, Luce, Sonia, Mandelbrot, Laurent, Lechenadec, Jerome, Cordier, Anne-Gael, Azria, Elie, Soulier, Jean, Cavazzana, Marina, Blanche, Stéphane, André-Schmutz, Isabelle
發表在 AIDS (2015)

Gene transfer into hematopoietic stem cells reduces HLH manifestations in a murine model of Munc13-4 deficiency

由 Soheili, Tayebeh, Durand, Amandine, Sepulveda, Fernando E., Rivière, Julie, Lagresle-Peyrou, Chantal, Sadek, Hanem, de Saint Basile, Geneviève, Martin, Samia, Mavilio, Fulvio, Cavazzana, Marina, André-Schmutz, Isabelle
發表在 Blood Adv (2017)

A human postnatal lymphoid progenitor capable of circulating and seeding the thymus

由 Six, Emmanuelle M., Bonhomme, Delphine, Monteiro, Marta, Beldjord, Kheira, Jurkowska, Monika, Cordier-Garcia, Corinne, Garrigue, Alexandrine, Dal Cortivo, Liliane, Rocha, Benedita, Fischer, Alain, Cavazzana-Calvo, Marina, André-Schmutz, Isabelle
出版 2007

Human T-Lymphoid Progenitors Generated in a Feeder-Cell-Free Delta-Like-4 Culture System Promote T-Cell Reconstitution in NOD/SCID/γc(−/−) Mice

由 Reimann, Christian, Six, Emmanuelle, Dal-Cortivo, Liliane, Schiavo, Andrea, Appourchaux, Kevin, Lagresle-Peyrou, Chantal, de Chappedelaine, Corinne, Ternaux, Brigitte, Coulombel, Laure, Beldjord, Kheira, Cavazzana-Calvo, Marina, Andre-Schmutz, Isabelle
出版 2012

MST1 mutations in autosomal recessive primary immunodeficiency characterized by defective naive T-cell survival

由 Nehme, Nadine T., Schmid, Jana Pachlopnik, Debeurme, Franck, André-Schmutz, Isabelle, Lim, Annick, Nitschke, Patrick, Rieux-Laucat, Frédéric, Lutz, Patrick, Picard, Capucine, Mahlaoui, Nizar, Fischer, Alain, de Saint Basile, Geneviève
出版 2011

An Optimized Lentiviral Vector Efficiently Corrects the Human Sickle Cell Disease Phenotype

由 Weber, Leslie, Poletti, Valentina, Magrin, Elisa, Antoniani, Chiara, Martin, Samia, Bayard, Charles, Sadek, Hanem, Felix, Tristan, Meneghini, Vasco, Antoniou, Michael N., El-Nemer, Wassim, Mavilio, Fulvio, Cavazzana, Marina, Andre-Schmutz, Isabelle, Miccio, Annarita
發表在 Mol Ther Methods Clin Dev (2018)

Generation of adult human T-cell progenitors for immunotherapeutic applications

由 Simons, Laura, Ma, Kuiying, de Chappedelaine, Corinne, Moiranghtem, Ranjita Devi, Elkaim, Elodie, Olivré, Juliette, Susini, Sandrine, Appourchaux, Kevin, Reimann, Christian, Sadek, Hanem, Pellé, Olivier, Cagnard, Nicolas, Magrin, Elisa, Lagresle-Peyrou, Chantal, Taghon, Tom, Rausell, Antonio, Cavazzana, Marina, André-Schmutz, Isabelle
發表在 J Allergy Clin Immunol (2018)

Loss of ARHGEF1 causes a human primary antibody deficiency

由 Bouafia, Amine, Lofek, Sébastien, Bruneau, Julie, Chentout, Loïc, Lamrini, Hicham, Trinquand, Amélie, Deau, Marie-Céline, Heurtier, Lucie, Meignin, Véronique, Picard, Capucine, Macintyre, Elizabeth, Alibeu, Olivier, Bras, Marc, Molina, Thierry Jo, Cavazzana, Marina, André-Schmutz, Isabelle, Durandy, Anne, Fischer, Alain, Oksenhendler, Eric, Kracker, Sven
發表在 J Clin Invest (2019)

Editing a γ-globin repressor binding site restores fetal hemoglobin synthesis and corrects the sickle cell disease phenotype

由 Weber, Leslie, Frati, Giacomo, Felix, Tristan, Hardouin, Giulia, Casini, Antonio, Wollenschlaeger, Clara, Meneghini, Vasco, Masson, Cecile, De Cian, Anne, Chalumeau, Anne, Mavilio, Fulvio, Amendola, Mario, Andre-Schmutz, Isabelle, Cereseto, Anna, El Nemer, Wassim, Concordet, Jean-Paul, Giovannangeli, Carine, Cavazzana, Marina, Miccio, Annarita
發表在 Sci Adv (2020)

RUNX1-dependent RAG1 deposition instigates human TCR-δ locus rearrangement

由 Cieslak, Agata, Le Noir, Sandrine, Trinquand, Amélie, Lhermitte, Ludovic, Franchini, Don-Marc, Villarese, Patrick, Gon, Stéphanie, Bond, Jonathan, Simonin, Mathieu, Vanhille, Laurent, Reimann, Christian, Verhoeyen, Els, Larghero, Jerome, Six, Emmanuelle, Spicuglia, Salvatore, André-Schmutz, Isabelle, Langerak, Anton, Nadel, Bertrand, Macintyre, Elizabeth, Payet-Bornet, Dominique, Asnafi, Vahid
出版 2014

RUNX1-dependent RAG1 deposition instigates human TCR-δ locus rearrangement

由 Cieslak, Agata, Le Noir, Sandrine, Trinquand, Amélie, Lhermitte, Ludovic, Franchini, Don-Marc, Villarese, Patrick, Gon, Stéphanie, Bond, Jonathan, Simonin, Mathieu, Vanhille, Laurent, Reimann, Christian, Verhoeyen, Els, Larghero, Jerome, Six, Emmanuelle, Spicuglia, Salvatore, André-Schmutz, Isabelle, Langerak, Anton, Nadel, Bertrand, Macintyre, Elizabeth, Payet-Bornet, Dominique, Asnafi, Vahid
發表在 J Exp Med (2014)

Plerixafor enables safe, rapid, efficient mobilization of hematopoietic stem cells in sickle cell disease patients after exchange transfusion

由 Lagresle-Peyrou, Chantal, Lefrère, François, Magrin, Elisa, Ribeil, Jean-Antoine, Romano, Oriana, Weber, Leslie, Magnani, Alessandra, Sadek, Hanem, Plantier, Clémence, Gabrion, Aurélie, Ternaux, Brigitte, Félix, Tristan, Couzin, Chloé, Stanislas, Aurélie, Tréluyer, Jean-Marc, Lamhaut, Lionel, Joseph, Laure, Delville, Marianne, Miccio, Annarita, André-Schmutz, Isabelle, Cavazzana, Marina
發表在 Haematologica (2018)